An experimental RNA therapy from Avidity Biosciences has early clinical trial results showing it reduced by half the expression of a gene at the root of a rare, inherited form of muscular dystrophy ...
These are the year's top 10 most-read muscular dystrophy news stories we published last year, each with a brief description.
Please provide your email address to receive an email when new articles are posted on . Cardiomyopathy in Duchenne muscular dystrophy possesses a unique pathophysiology. Integrated wall stress can be ...
On Monday, the U.S Food and Drug Administration (FDA) lifted the clinical hold on Entrada Therapeutics, Inc. (NASDAQ:TRDA) ENTR-601-44. The agency issued the hold in December 2022. In November 2023, ...
At the upcoming annual meeting of the American Society of Gene and Cell Therapy, scientists from Huidagene Therapeutics will share an update on the development of their ...
Editor’s note: This is an automatically generated transcript. Please notify [email protected] if there are concerns regarding accuracy of the transcription. One key aspect of the journey for a person ...
Oculopharyngeal muscular dystrophy (OPMD) is a rare inherited disorder that causes weakness in the eye and throat muscles. It may lead to drooping eyelids and swallowing difficulties. Muscular ...
Congenital muscular dystrophy (CMD) is a disease that affects certain muscles. Individuals with CMD may experience symptoms such as muscle weakness and joint problems. “Congenital” means present since ...
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