More than 9 out of 10 Alzheimer's cases could be driven by specific variations in a single gene and the protein it produces, ...

The FDA granted fast track status to VectorY’s VTx-002, an antibody gene therapy targeting TDP-43 protein aggregates in ALS.

UCSF scientists engineered old fibroblast cells to turn their genes on and off in the same way as young fibroblasts. The old ...

The first patient has been dosed in a Phase 2 clinical trial testing RAG-17 in people with ALS who carry mutations in the ...

Precision and timing of gene expression is essential for normal biological functions and, when disrupted, can lead to many ...

In a groundbreaking study published in the in Proceedings of the National Academy of Sciences (PNAS), scientists at Pacific ...

A new LUMC study has changed our understanding of how cells work. Researchers have discovered that the CFAP20 protein acts as ...

We know the genes, but not their functions—to resolve this long-standing bottleneck in microbial research, a joint research ...

A research team led by Zhiping Weng, Ph.D., and Jill Moore, Ph.D."18, at UMass Chan Medical School, has nearly tripled the ...

Identifying genes that control protein levels could provide insight into disease development and progression. However, genetic analyses such as genome-wide associated studies identify regions ...