New one-dose treatment edits a gene in the liver, disabling the ANGPTL3 protein and significantly lowers cholesterol.

Non-protein-coding genes have been linked to a hereditary condition, retinitis pigmentosa, that causes progressive blindness.

An international research team has succeeded in deciphering a key mechanism that controls the growth of pancreatic cancers.

Dr Mark Kris discusses the increasing precision of lung cancer therapies and the need for additional testing to find ...

The new molecules selectively reduced inflammatory signaling in human immune cells without affecting other immune pathways.

Tweaking a pattern of wound healing established millions of years ago may enable scar-free injury repair after surgery or ...

The FDA granted orphan drug designation to zavabresib, an investigational therapy for the treatment of myelofibrosis, a rare ...

A team of bioengineers at the Indian Institute of Technology (IIT) Bombay has developed new smart platforms --BrainProt and DrugProtAI -- that unify data on scattered brain diseases to help ...

Mumbai, Jan 22: A team of scientists at the Indian Institute of Technology (IIT) Bombay, working with researchers from several institutions in India and abroad, has developed BrainProt v3.0, an ...

Could this mark a shift in how we think about cancer therapy? At least in the laboratory, evidence suggests it may be . An ...

If you are like a lot of people, you might be anxious about the risk of getting dementia as you age. The lifetime risk of ...

A chain of immune reactions in the gut—driven by a key signaling protein and a surge of white blood cells from the bone marrow—may help explain why people with inflammatory bowel disease (IBD) have a ...