Sarepta Therapeutics SRPT announced positive three-year top-line data from Part 1 of the phase III EMBARK study, evaluating ...
Keros Therapeutics KROS is a clinical-stage biopharmaceutical company developing innovative therapies for patients with ...
Sarepta says effects of Duchenne muscular dystrophy gene therapy were durable three years after treatment; More biotech ...
Researchers at Kumamoto University in Japan have discovered that iron supplements may help reduce muscle damage and improve ...
Dyne Therapeutics leverages its FORCE platform to target genetically driven muscle diseases. Read why I am bullish about DYN ...
After a roller coaster of a year for Duchenne muscular dystrophy (DMD) gene therapy Elevidys (delandistrogene moxeparvovec), Sarepta Therapeutics Inc. looks to focus on the efficacy narrative in 2026, ...
In his CEO Commentary, Frederic Revah, Ph.D., underscores the dedication, expertise and successes of Genethon's 240 scientists and professional staff as they pursue new gene therapy treatments for ...
Discusses 3-Year Topline Results From EMBARK Phase 3 Trial of ELEVIDYS in Duchenne Muscular Dystrophy January 26, ...
After a spate of patient deaths in 2025 linked to the company’s Duchenne gene therapy, Sarepta shared new data showing benefits of the therapy three years after dosing.
Sarepta Therapeutics' gene ‌therapy for Duchenne muscular dystrophy slowed disease progression and showed sustained benefit ...
Sarepta shares jump 5% after hours as company sets January 26 for 3-year Elevidys data following FDA safety warning and label restrictions.
Sarepta is on an urgent mission: engineer precision genetic medicine for rare diseases that devastate lives and cut futures short. We hold leadership positions in Duchenne muscular dystrophy (Duchenne ...